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Patient Focus

Ester and her dog kneel on the side of a country path with green fields stretching into the distance October 24, 2026 Celebrating Caregivers – "The People Who Keep Showing Up for You" Read Ester's story and insights on caregiving while living with hereditary ATTR amyloidosis, including lessons on resilience, support, and self-care. Read More ›
Former professional football player Pete Shaw holding a football on a football field October 15, 2026 The Signs Were There: How Pete Shaw and His Team Faced an Unexpected Opponent For former professional football player Pete Shaw, recognizing the signs of hATTR-CM meant looking beyond the expected. Read his story and path to answers. Read More ›
Puzzle pieces featuring protein structures, a digital heart illustration, healthcare analytics, and a clinician, representing collaboration in ATTR research, diagnosis, and patient care August 26, 2026 Advancing Earlier Diagnosis and Coordinated Care in ATTR-CM For patients with transthyretin amyloidosis with cardiomyopathy (ATTR-CM), the path to effective care often begins with a challenge: receiving the right diagnosis before the disease irreversibly advances. Read More ›
TRITON CM clinical trial article March 27, 2026 Five Things to Know about TRITON-CM & How Community Insight is Shaping the Future of ATTR- ... TRITON-CM, Alnylam's Phase 3 clinical trial evaluating nucresiran, a third-generation investigational RNAi therapeutic for transthyretin amyloidosis with cardiomyopathy (ATTR-CM), represents one of the largest global studies ever conducted in this disease. Read More ›
Alnylam WAD 2025 October 24, 2025 Looking Beyond the Clinic: Putting Patients at the Center of Holistic Care in Transthyreti ... Enhancing understanding of this life-threatening disease and ensuring that care reflects the realities of those living with it are vital goals shared across the Read More ›
Alnylam Health Literacy October 20, 2025 Alnylam’s Commitment to Health Literacy for All As a patient-centric organization, Alnylam is fully committed to promoting the principles of health literacy as an integral part of our innovation and culture. Read More ›
ATTR holistic care September 6, 2023 First Consensus Recommendations for Holistic Care of People Living With Hereditary ATTR Am ... The Amyloidosis Alliance has published the first-ever consensus recommendations for patient- and family-centred holistic care in ATTRv. Read More ›
Clement Family Newsroom Article February 28, 2023 The Importance of Self-Advocacy: Supporting Patients and Caregivers in Their Rare Disease ... Rare Disease Day unites the community to spread awareness and support the millions of people worldwide living with with a rare disease. Read More ›
Alnylam VBNF May 9, 2022 Building a Collaborative Framework for Facilitating Patient Access to Innovative Therapies Alnylam worked with leading European economists and other healthcare experts to develop what we call the Value-Based Negotiation Framework (VBNF) to help... Read More ›
Two of Me Living with Porphyria April 2, 2022 The Making of Two of Me: Living with Porphyria Cynthia Lowen, Emmy-nominated filmmaker, talks about the making of Two of Me: Living with Porphyria. Read More ›
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